Mississippi Center for Advanced Medicine
Hereditary Angioedema
Obesity/Metabolic Disorders
Hemophilia B
- A Study to Evaluate the Efficacy and Safety of Factor IX Gene Therapy With PF-06838435 in Adult Males With Moderately Severe to Severe Hemophilia B (BENEGENE-2)
- Long-term Safety and Efficacy Study and Dose-Escalation Substudy of PF 06838435 in Individuals With Hemophilia B
- A Study to Learn About the Safety and Effectiveness of the Study Medicines Called Giroctocogene Fitelparvovec and Fidanacogene Elaparvovec
Hemophilia A or B
Sickle Cell Disease
- A Study Evaluating the Efficacy and Safety of Mitapivat (AG-348) in Participants With Sickle Cell Disease (RISE UP)
- Research Study Investigating How Well NDec Works in People With Sickle Cell Disease (ASCENT1)
- GBT021601-021: A Study in Adult and Pediatric Participants With SCD
- Oxbryta® Product Registry An Observational Study Designed to Evaluate the Effect of Oxbryta in Individuals With SCD (PROSPECT)
- A Study Evaluating the Efficacy, Safety, Pharmacokinetics, and Pharmacodynamics of Crovalimab as Adjunct Treatment in Prevention of Vaso-Occlusive Episodes (VOE) in Sickle Cell Disease (SCD) (CROSSWALK-c)
Severe Von Willebrand Disease
Rare Coaguation Disorders
Non-Neoplastic Hematologic Disorders
Louisiana Center for Advanced Medicine
Hemophilia B
Hemophilia A or B
- Compassionate Use of Concizumab if You Have Hemophilia
- A Study of the Safety of SEVENFACT® for the Treatment of Bleeding Events in Patients with Hemophilia A or B with Inhibitors
Severe Von Willebrand Disease
